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Arimoclomol Citrate

Tier C — Watch / trade

Arimoclomol Citrate

Orphazyme A/S
Originator
2024
First approval
-
Expiry (public)
No sales data
Peak sales
Small molecule
Type

Targets:Molecular chaperones

Brand:Miplyffa

Indications (approved):C型尼曼匹克病

Regional status

US
Approved
2024-09-20
EU
Filed / under review
2022-02-17
China
-
Japan
-

Factories producing this API6

Factories registered as producing this API in our sourcing network (RFQ records + product master), sorted by RFQ activity; the snapshot carries no cost or customer data.

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Synthetic routes & intermediates3 routes

Originator routes × 0Optimised (non-patent) × 3Process routes × 0

Routes are ordered originator first, then optimised / process (non-patent) routes; each lists steps, overall yield and the intermediate table (code / CAS / name) — ready for supplier sourcing and RFQ. Rendered by this site from structured data; no third-party route graphics used.

OptimisedRoute 1Steps 6 · Total yield /
(I)320339-3-a574-66-3(II)320339-3-a,(II)320339-3-b115314-17-5(III)320339-3-a2161374-86-1(IV)320339-3-a,(IV)320339-3-b110-89-4(IX)320339-3-a,(IX)320339-3-b—(V)320339-3-a2161374-90-7(VI)320339-3-a2161374-94-1(VII)320339-3-a14906-64-0(VIII)320339-3-a—API · Arimoclomol Citrate
CodeCAS No.Intermediate
(I)320339-3-a574-66-3Benzophenone oxime
(II)320339-3-a,(II)320339-3-b115314-17-5(R)-(-)-Glycidyl m-nitrobenzenesulfonate
(III)320339-3-a2161374-86-1N-[[(2R)-Oxiran-2-yl]methoxy]-1,1-diphenylmethanimine
(IV)320339-3-a,(IV)320339-3-b110-89-4Azacyclohexane
(IX)320339-3-a,(IX)320339-3-b-N-[(2R)-2-Hydroxy-3-(piperidin-1-yl)propoxy]-1-oxo-1lambda5-pyridine-3-carboximidoyl chloride
(V)320339-3-a2161374-90-7(2R)-1-[[(Diphenylmethylidene)amino]oxy]-3-(piperidin-1-yl)propan-2-ol
(VI)320339-3-a2161374-94-1(2R)-1-(Aminooxy)-3-(piperidin-1-yl)propan-2-ol--hydrogen chloride (1/1)
(VII)320339-3-a14906-64-03-cyano-1-oxidopyridin-1-ium
(VIII)320339-3-a-N'-[(2R)-2-Hydroxy-3-(piperidin-1-yl)propoxy]-1-oxo-1lambda5-pyridine-3-carboximidamide
OptimisedRoute 2Steps 4 · Total yield /
(II)320339-3-a,(II)320339-3-b115314-17-5(IV)320339-3-a,(IV)320339-3-b110-89-4(IX)320339-3-a,(IX)320339-3-b—(X)320339-3-b1594-58-7(XI)320339-3-b—(XII)320339-3-b—(XIII)320339-3-b496816-63-8API · Arimoclomol Citrate
CodeCAS No.Intermediate
(II)320339-3-a,(II)320339-3-b115314-17-5(R)-(-)-Glycidyl m-nitrobenzenesulfonate
(IV)320339-3-a,(IV)320339-3-b110-89-4Azacyclohexane
(IX)320339-3-a,(IX)320339-3-b-N-[(2R)-2-Hydroxy-3-(piperidin-1-yl)propoxy]-1-oxo-1lambda5-pyridine-3-carboximidoyl chloride
(X)320339-3-b1594-58-7N'-hydroxypyridine-3-carboximidamide
(XI)320339-3-b-N'-[[(2R)-Oxiran-2-yl]methoxy]pyridine-3-carboximidamide
(XII)320339-3-b-N'-[(2R)-2-Hydroxy-3-(piperidin-1-yl)propoxy]pyridine-3-carboximidamide
(XIII)320339-3-b496816-63-8N-[(2R)-2-hydroxy-3-(piperidin-1-yl)propoxy]pyridine-3-carbonimidoyl chloride
OptimisedRoute 3Steps 5 · Total yield /
(I)320339-4-a2102429-29-6(II)320339-4-a15285-58-2(III)320339-4-a—(IV)320339-4-a—(V)320339-4-a—(VI)320339-4-a—API · Arimoclomol Citrate
CodeCAS No.Intermediate
(I)320339-4-a2102429-29-63-(N'-Hydroxycarbamimidoyl)-1-oxidopyridin-1-ium
(II)320339-4-a15285-58-22-Hydroxy-4-azaspiro[3.5]nonan-4-ylium chloride
(III)320339-4-a-3-{N'-[2-Hydroxy-3-(piperidin-1-yl)propoxy]carbamimidoyl}-1-oxidopyridin-1-ium
(IV)320339-4-a-3-[1-Chloro-1-[2-hydroxy-3-(1-piperidinyl)propoxyiminomethyl]pyridine 1-oxide
(V)320339-4-a-(2R,3R)-2,3-Bis(benzoyloxy)butanedioic acid N-[(2R)-2-hydroxy-3-(piperidin-1-yl)propoxy]-1-oxo-1lambda5-pyridine-3-carboximidoyl chloride
(VI)320339-4-a-N-[(2R)-2-Hydroxy-3-(piperidin-1-yl)propoxy]-1-oxo-1lambda5-pyridine-3-carboximidoyl chloride

Frequently asked questions

What are the approved indications of Arimoclomol Citrate?

Approved indications include: C型尼曼匹克病.

When does the Arimoclomol Citrate patent expire?

No public expiry year is available for Arimoclomol Citrate yet; this page updates once verified.

How many synthesis routes are recorded for Arimoclomol Citrate?

3 synthesis routes are recorded; the shortest is 4 steps with / total yield. Intermediates in each route carry codes and CAS numbers.

Where can I buy Arimoclomol Citrate intermediates?

All intermediates in Arimoclomol Citrate routes have CAS profiles — you can submit an RFQ per CAS and it enters the Unibest matching pool.

How do I get a quote for Arimoclomol Citrate intermediates?

Open the CAS profile of the target intermediate from this page, or submit an RFQ directly — the CAS enters the matching flow automatically and the supply network responds with quotes.

Source: cross-verified data (structured fields only) · 2026-09-29